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Dernières publications
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Valentina Taglietti, Kaouthar Kefi, Lea Rivera, Oriane Bergiers, Nastasia Cardone, et al.. Thyroid-stimulating hormone receptor signaling restores skeletal muscle stem cell regeneration in rats with muscular dystrophy. Science Translational Medicine, 2023, 15 (685), ⟨10.1126/scitranslmed.add5275⟩. ⟨hal-04150315⟩
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A. Morin, Amalia Stantzou, Olga N. Petrova, John C.W. Hildyard, T. Tensorer, et al.. Dystrophin myonuclear domain restoration governs treatment efficacy in dystrophic muscle. Proceedings of the National Academy of Sciences of the United States of America, 2023, 120 (2), ⟨10.1073/pnas.2206324120⟩. ⟨hal-04122777⟩
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Valentina Taglietti, Kaouthar Kefi, Iwona Bronisz-Budzyńska, Busra Mirciloglu, Mathilde Rodrigues, et al.. Duchenne muscular dystrophy trajectory in R-DMDdel52 preclinical rat model identifies COMP as biomarker of fibrosis. Acta Neuropathologica Communications, 2022, 10 (1), ⟨10.1186/s40478-022-01355-2⟩. ⟨hal-03828280⟩
Chiffres clés
48
Publications avec texte intégral
Open Access
67 %
Mots clés
Muscle Biology
Myogenesis
Duchenne muscular dystrophy DMD
Gene expression
Antisense oligonucleotides
DMD
Dystrophin central domain
Molecular Sequence Data
Muscular dystrophy
Multi resolution modeling
Exon skipping
Multiresolution modeling
Centronuclear myopathy
Duchenne DMD dystrophy
Cell Line
Allele‐specific silencing therapy
Dystrophie Musculaire de Duchenne DMD
Base Sequence
Activin Receptors
Dystrophie musculaire de Becker
Male
Animals
Muscular Dystrophy
Immunoglobulin Fc Fragments/pharmacology
Animal/physiopathology
Myotendinous junction
Dystrophine
LncRNA
LKB1
Gene modifiers
Autophagy
Becker BMD muscular dystrophy
Génomique
DHPR α1S
Metabolism
Genomic
Muscular Atrophy
Muscle
Cachexia
NAD+
Cardiomyopathie
Duchenne muscular dystrophy
Inbred C57BL
Ex-vivo
Long noncoding RNA
Dystrophin
Mice
Skeletal muscle
Cell Biology
Hepatocellular carcinoma
Diseases
Becker muscular dystrophy BMD
CaVβs
Gene Expression Regulation/drug effects
Dynamin 2
Liver
Drp1
Cultured
CaV subunits
CD38
CTNNB1
Hear
L-Type
Knockout
Inhibitors
Muscle Strength
Becker muscular dystrophy
Dystrophin-EGFP
Muscle development
Cells
Human Umbilical Vein Endothelial Cells
NNOS
LncARN
Cell homeostasis
Long QT
Delivery
Becker muscular dystrophy BMD Duchenne muscular dystrophy DMD miRNA nNOS
Humans
BMD
Mdx mouse
Inbred mdx
DMO
Multi exon skipping
Dystrophy
Invivo
MES
Energy Metabolism/drug effects
Muscles/physiopathology
Modificateurs de gènes
Cardiomyopathy
Clinical trials
Morphogenesis
Molecular docking
Dystrophie Musculaire de Becker BMD
Mitochondrial fission
Homeostasis
Calcium
MiARN
Epigenetics
Calcium Channels