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Glucocorticoids Myotonic dystrophy type 1 Cell model ARN PCR Alternative splicing Myotonic Dystrophy Type 1 Desmin Myotonic dystrophy Dystrophin KNOCKOUT MICE Acetylcholinesterase deficiency Gene Therapy Motoneuron DMPK Cardiac muscle MBNL Knockout Genotype phenotype correlation CRISPRi Oligodendrocytes Muscle DM1 GSK3␤ Myelin Animals Diaphragm Duchenne muscular dystrophy Glutamate Gene editing Humans Maximal force CTG repeat instability Dystrophie myotonique Therapy Quantitative microdialysis Glucocorticoid-receptor Neuron BIOLOGIE MOLECULAIRE Skeletal muscle Myostatin In vivo Transgenic mouse model GABA Brain Central nervous system Dystrophie Myotonique CTG repeat contractions Cell culture model Trinucleotide repeat expansion Male Astrocyte Heart failure Mice Muscular dystrophy Dynamin 2 Centronuclear myopathy ACETYLCHOLINESTERASE CTG repeats Exercice Dilated cardiomyopathy Gene therapy Mouse models Heart Transgenic mouse Expression Intermediate filament Oligodendrocyte PacBio Aging Acetylcholinesterase knockout mouse Lc3 Brain dysfunction CONGENITAL MYATHENIC SYNDROME Autophagy Glial cells RNA biology Myotonic Dystrophy Hypoxia Myotonic Dystrophy type 1 Astrocytes RNA splicing Cytoskeleton AAV Cell penetrating peptide Fibrosis Myotonic dystrophy mouse models DMSXL mice Transcriptomics Antisense oligonucleotide CRISPR/Cas9 Mouse model Acute coronary syndrome Long read sequencing CMS RNA interference Exercise Thérapie génique Antisense oligonucleotides Trinucleotide Repeat Expansion